20.02.23

San Raffaele-Telethon Institute receives European funds to study how blood is formed

Andrea Ditadi awarded an ERC Consolidator Grant worth 2 million euro

From Research

17.12.22

New frontiers for gene therapy

At the San Raffaele-Telethon Institute in Milan researchers are working to apply gene therapy, an approach that has already given important results, to even more diseases optimizing development times and costs.

From Research

16.05.22

Fondazione Cariplo and Fondazione Telethon: 24 projects funded with more than 5 million euros for basic research in the field of rare diseases

Winners of the 2021 Call for Basic Research have been selected from all over Italy to study the still obscure portions of our genetic heritage.

From Research

29.04.22

Generating blood in vitro: a new piece of the puzzle

An important contribution to the elucidation of the mechanisms through which blood stem cells arise during embryonic life from a study conducted by the San Raffaele Telethon Institute for Gene Therapy.

From Research

05.04.22

Gene therapy targeted to the brain: a complex but not impossible challenge

Angela Gritti from the San Raffaele Telethon Institute of Milan talks about the efforts of applying gene therapy to one of the most difficult body organs to access.

From Research

09.03.22

Aicardi-Goutières syndrome: when the immune system detects viruses where there are none

An interview with Anna Kajaste-Rudnitski from the San Raffaele Telethon Institute for Gene Therapy in Milan, author of a study that gives new insights into this rare syndrome and provides also useful information to investigate the interaction between the immune system and viruses, including Sars-CoV-2.

From Research

09.11.20

A novel finding on Kabuki syndrome, a rare genetic disease

The research, coordinated by the University of Trento, has recreated for the first time the pathological condition in a test tube discovering what happens in the cell nucleus and what hinders the formation of cartilages and bones.

From Research

16.10.20

Orchard Therapeutics Receives Positive CHMP Opinion for LibmeldyTM for the Treatment of Early-Onset Metachromatic Leukodystrophy (MLD)

First therapy recommended for EU approval for eligible patients with confirmed diagnosis of late infantile or early juvenile MLD variants.

From Research

07.09.20

Osteopetrosis: new opportunity of treatment thanks to a licensing agreement

SiSaf announces a research collaboration and licensing agreement with the University of L’Aquila for the treatment of the debilitating bone disease, Autosomal Dominant Osteopetrosis Type 2.

From Research

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