We want to advance biomedical research toward the treatment of rare genetic diseases.
Often neglected by large public or industrial investment schemes, and the poor relation when it comes to research and drug treatments - rare genetic conditions are not statistically relevant when considered individually. But every life counts for us.
That is why we have chosen to prioritise these diseases and give attention to those who are ignored.
What is our response to this silent emergency?
- We prioritise pathologies neglected by investments.
- We select the best research projects in Italy using a transparent method that rewards merit and excellence.
- We constantly support our institutes in Milan and Pozzuoli, centres of excellence that attract researchers from all over the world.
- We involve all Italians in the search for a cure, informing those who help us about the use of the funds raised during the year.
We develop innovative treatments that are already saving the lives of children such as Ana Carolina
We provide a diagnosis for patients such as Nina suffering from extremely rare and unknown conditions
We work continually to improve the lives of patients such as Michele with neuromuscular conditions
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Funding research is not enough: we want to turn the results of excellent scientific research into treatments that are accessible to all patients. Because everyone has the right to a cure.
A vision that has been becoming a reality for some years now, thanks to innovative therapies that are attracting the attention of more and more pharmaceutical groups, the development of partnerships with public and private health institutions so that our work does not stop at the successful scientific result, but becomes truly accessible to every patient.