To secure the future of research on rare genetic diseases, we established two Institutes in Italy, now internationally recognized as centers of excellence. They bring together leading scientists, hospitals, academia, and industry in a collaborative ecosystem that drives innovation from discovery to pioneering therapies.

Headed by Luigi Naldini, SR-Tiget is a world leader for gene therapy: the therapy for the treatment of ADA-SCID is one of the first examples of effective gene therapy in the world.

Headed by Alberto Auricchio, Tigem is an institute where researchers could focus on studying the mechanisms underlying genetic diseases and on developing innovative therapeutic strategies.