News
14.11.25
CHMP positive opinion for Waskyra™, a gene therapy for the treatment of Wiskott-Aldrich syndrome (WAS)
Announced the positive opinion issued by the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA), recommending marketing authorisation in the European Union for Waskyra™, an ex vivo gene therapy for Wiskott-Aldrich Syndrome.
13.11.25
Cracking the Code: IPEX, FOXP3 and the Path to Gene Therapy
Discover how SR-TIGET scientists advanced the genetics of peripheral immune tolerance, from FOXP3 and IPEX to gene therapy using lentiviral vectors.
04.11.25
The origins of peripheral immune tolerance: SR-TIGET's contribution to a Nobel-winning field
Discover how SR-TIGET scientists helped shape the science of peripheral immune tolerance, from the discovery of Treg and Tr1 cells to early gene therapy.
16.10.25
Attya Omer Named Runner-Up in the Nature Inspiring Women in Science Awards
The scientist of SR-TIGET and Università Vita-Salute San Raffaele recognized internationally for her vision in advancing gene therapy and inspiring women in science.
23.09.25
The Armenise-Harvard Foundation invests one million dollars in brain research
Thanks to the Career Development Award, neuroscientist Gabriele Ciceri will establish a new laboratory at the San Raffaele-Telethon Institute for Gene Therapy.
28.08.25
How Newborn Liver Cells Shape Growth and Future Treatments
A discovery at SR-Tiget reveals the key liver cells driving organ growth and advancing pediatric gene therapy
06.08.25
New 3D imaging tech revolutionizes lysosomal disease research
A new HTFC method allows live 3D lysosome imaging, with applications in Niemann-Pick C1 diagnosis and monitoring
30.07.25
Usher Syndrome: Promising Preliminary Results from Gene Therapy
An experimental gene therapy developed at the TIGEM has shown encouraging clinical results in patients with Usher syndrome type 1B.
17.06.25
TIGEM secures ERC grant for programmable gene‑circuit therapy
di Bernardo’s DIMERCIRCUITS integrates AI and synthetic biology to advance precision gene therapy.
